Protein Delivery Vehicles (PDVs) delivered in vivo CRISPR therapy

 

Stromal corneal dystrophy

Undisclosed

Undisclosed

Lipid nanoparticles (LNPs) delivered in vivo CRISPR therapy

Rare disease

Undisclosed

Metabolic disease

Undisclosed

Program

Discovery

Preclinical

IND-enabling

Clinical

Approval

Available for out-licensing

Available for out-licensing